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A Medscape supported initiative with additional support provided by:
Actelion Pharmaceuticals Ltd, a Janssen pharmaceutical company of Johnson & Johnson; Amryt; Alexion Pharmaceuticals, Inc; Ipsen; Mirum Pharmaceuticals; Novartis; Roche; Takeda AG
GP, Leeds and PRISM Group
Clinical Lead at Mendelian Health
University of Nottingham, United Kingdom
Professor of Clinical Medicine
Divisions Endocrinology and Metabolism and Geriatrics
Director, Fellowship in Metabolic Bone Disease
Director, Calcium Disorders Clinic
McMaster University
Hamilton, Ontario, Canada
Professor of Medicine
Chief, Division of Pulmonary and Critical Care Medicine
Weill Cornell Medical Center
New York, New York
Chief Executive of Medics4RareDiseases
UK
Associate Professor of Clinical Pediatrics and Neurology
The Ohio State University College of Medicine
Section Chief
Pediatric Neurology
Nationwide Children's Hospital
Columbus, Ohio, United States
Professor of Hematology, Oncology
Hannover Medical School, Germany