Clinical Advances in
After many years, gene therapy in patients with hemophilia has started to show promising results in alleviating symptoms and improving the disease phenotype. This collection of programs provides important information on the science behind gene therapy for hemophilia, the latest safety and efficacy data from clinical trials, and the potential role for gene therapy in addressing the challenges of current treatment methods.
Supported by an independent educational grant from
BioMarin
Presented through a collaboration between Medscape and
Supported by an independent educational grant from
BioMarin
Presented through a collaboration between Medscape and
Supported by an independent educational grant from
BioMarin
Presented through a collaboration between Medscape and
Steering Committee Chair
Professor of Haemostasis and Thrombosis, Barts and the London School of Medicine and Dentistry, London, United Kingdom
Professor of Haematology, Faculty of Health Sciences, Department of Molecular Medicine and Haematology, University of the Witwatersrand; Head of Clinical Haematology Ward and Service, Charlotte Maxeke Johannesburg Academic Hospital, Johannesburg, South Africa
Assistant Professor; Director, IHTC Hemocentro UNICAMP, University of Campinas; Director, WFH International Hemophilia Training Center, Sao Paulo, Brazil
Professor of Internal Medicine, University of Milan; Director, Angelo Bianchi Bonomi Hemophilia and Thrombosis Center, Milan, Italy
Professor of Pediatrics and Pathology, University of Michigan, Ann Arbor, Michigan, United States
Associate Member; Director of Clinical Hematology; Director, Pediatric Hemophilia Treatment Center, Department of Hematology, St. Jude Children's Research Hospital, Memphis, Tennessee, United States